@article{friede:inserm-02456642,
TITLE = {Approaches to sample size calculation for clinical trials in rare diseases},
AUTHOR = {Friede, Tim and Alberti, Corinne and Benda, Norbert and Comets, Emmanuelle and Dmitrienko, Alex and Graf, Alexandra and G{\"u}nhan, Burak K{\"u}rsad and Lentz, Frederike and Ondra, Thomas and R{\"o}ver, Christian and Toumazi, Artemis and Unkel, Steffen and Ursino, Moreno and Wassmer, Gernot and Miller, Frank and Zohar, Sarah and Stallard, Nigel and Madan, Jason and Posch, Martin and Hee, Siew Wan and Pearce, Michael and V{\aa}ger{\"o},
M{\aa}rten and Day, Simon},
URL = {https://inserm.hal.science/inserm-02456642},
JOURNAL = {Pharmaceutical Statistics},
PUBLISHER = {Wiley},
VOLUME = {17},
NUMBER = {3},
PAGES = {214-230},
YEAR = {2018},
MONTH = May, DOI = {10.1002/pst.1848},
HAL_ID = {inserm-02456642},
HAL_VERSION = {v1},
}
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