@article{domenger:inserm-01734756,
TITLE = {RNA-Seq Analysis of an Antisense Sequence Optimized for Exon Skipping in Duchenne Patients Reveals No Off-Target Effect},
AUTHOR = {Domenger, Claire and Allais, Marine and Fran{\c c}ois, Virginie and Leger, Adrien and Lecomte, Emilie and Montus, Marie and Servais, Laurent and Voit, Thomas and Moullier, Philippe and Audic, Yann and Le Guiner, Caroline},
URL = {https://inserm.hal.science/inserm-01734756},
JOURNAL = {Molecular Therapy - Nucleic Acids},
PUBLISHER = {Elsevier},
VOLUME = {10},
PAGES = {277 - 291},
YEAR = {2018},
MONTH = Mar, DOI = {10.1016/j.omtn.2017.12.008},
KEYWORDS = {exon skipping ; Duchenne ; U7snRNA ; off-target ; RNA sequencing},
PDF = {https://inserm.hal.science/inserm-01734756/file/2018%20Domenger%20et%20al.pdf},
HAL_ID = {inserm-01734756},
HAL_VERSION = {v1},
}
Affichage BibTex